Promising new gene therapies for sickle cell remain unavailable in countries where they are needed most
Gautam Dongre’s two children in India and Pascazia Mazeze’s son in Tanzania live with an inherited blood disorder that turns blood cells into instruments of pain. Now that new gene therapies promise a cure for sickle cell disease, Dongre says he’s “praying for the cure to come to us.” But experts say a one-time treatment… Read More »