Tag Archives: Vertex Pharmaceuticals

FDA approves 2 gene therapies for sickle cell. One of the first to use the CRISPR editing tool

Regulators approved two gene therapies for sickle cell disease on Friday. Doctors hope they may be able to cure painful, inherited blood disease that mostly affects black people in the US The Food and Drug Administration said the one-time treatments can be used for patients ages 12 and older with severe forms of the disease.… Read More »